CF Community Archives - Page 13 of 16 - The Boomer Esiason Foundation

March 19, 2019

SOURCEKalydeco, a treatment for cystic fibrosis developed by Vertex Pharmaceuticals VRTX +2.40% with support from the Cystic Fibrosis Foundation , was awarded the first Forbes Breakthrough Drug Award today for dramatically improving the lives of patients and conquering a scientific challenge that had vexed researchers...

Raptor Announces Qualified Infectious Disease Product

by BEF

CF Community, CF News, Research, Therapies

March 19, 2019

SOURCE: Original Press Release Raptor Announces Qualified Infectious Disease Product (QIDP) Designation for MP-376, Inhaled LevofloxacinGranted for Three Distinct Indications: Chronic Pulmonary Infections Due to Pseudomonas Aeruginosa in Patients with Cystic Fibrosis and in Patients with Non-Cystic Fibrosis Bronchiectasis as well as in Patients with Nontuberculous MycobacteriaPre-NDA Discussion...

CF Mutation May Change How Proteins Communicate via CF News Today

by BEF

CF Community, CF News, Research

March 19, 2019

Original Post Protein interactions could be misdirected in people with cystic fibrosis (CF), causing a loss of normal protein function, according to researchers from the Scripps Research Institute (TSRI) in San Diego, California. The new study, titled “∆F508 CFTR interactome remodelling promotes rescue of cystic fibrosis“...

Vertex Announces Significant Progress in Development via Vertex

by BEF

CF Community, CF News, Research, Therapies

March 19, 2019

SOURCE - OFFICIAL PRESS RELEASE Vertex Announces Significant Progress in Its Development Efforts to Treat the Cause of Cystic Fibrosis in the Vast Majority of People with the Disease-Two next-generation correctors to enter clinical development in November; studies of a triple combination of a next-generation corrector...

ORKAMBI™ Is Now FDA Approved!

by BEF

CF Community, CF News, Research, Therapies

March 19, 2019

ORKAMBI is a prescription medicine used for the treatment of cystic fibrosis (CF) in patients age 12 years and older who have two copies of the F508del mutation (F508del/F508del) in their CFTR gene. ORKAMBI should not be used in patients other than those who have two...

FDA Panel Recommends Approval of ORKAMBI™ via Vertex

by BEF

CF Community, CF News, Research, Therapies

March 19, 2019

SOURCE --- Please read the original press release here --- SOURCE FDA decision expected by July 5, 2015 PDUFA date Approximately 8,500 people with cystic fibrosis in the U.S. have two copies of the F508del mutation and are ages 12 and older BOSTON--(BUSINESS WIRE)-- Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX)...

Yale scientists use gene editing to correct mutation in cystic fibrosis via Yale News

by BEF

CF Community, CF News, Research, Therapies

March 19, 2019

SOURCE Yale researchers successfully corrected the most common mutation in the gene that causes cystic fibrosis, a lethal genetic disorder. The study was published April 27 in Nature Communications. Cystic fibrosis is an inherited, life-threatening disorder that damages the lungs and digestive system. It is most commonly caused...

New antibiotic teixobactin kills drug-resistant superbugs, study says via LA Times

by BEF

CF Community, CF News, Research, Therapies

March 19, 2019

SOURCE: LA TIMES Using soil from a grassy field in Maine and a miniaturized diffusion chamber, scientists have cultivated a microbe that could help tame the spread of antibiotic-resistant superbugs. When tricked into growing in a lab, the microbe makes a compound that kills strains of tuberculosis,...

CFF Announces Unprecedented Acceleration and Expansion of CF Research, Care and Patient Programs

by BEF

CF Community, CF News, Research

March 19, 2019

SOURCE: CFF.org The Cystic Fibrosis Foundation today announced an unprecedented acceleration and expansion of its research, care and patient programs for the CF community. This action is possible as a result of the sale of the Foundation’s royalty rights to CF treatments developed by Vertex Pharmaceuticals...

FDA Recommends Approval of KALYDECO for Use in People with CF R117H Mutation

by BEF

CF Community, CF News, Research, Therapies

March 19, 2019

SOURCE: VERTEX PRESS RELEASE FDA Advisory Committee Recommends Approval of KALYDECO® (ivacaftor) for Use in People with Cystic Fibrosis Ages 6 and Older Who Have the R117H Mutation BOSTON--(BUSINESS WIRE)-- Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) today announced that the U.S. Food and Drug Administration's Pulmonary Allergy Drugs...

CF Community

Kalydeco Wins First Annual Forbes Breakthrough Drug Award via Forbes.com

Raptor Announces Qualified Infectious Disease Product

CF Mutation May Change How Proteins Communicate via CF News Today

Vertex Announces Significant Progress in Development via Vertex

ORKAMBI™ Is Now FDA Approved!

FDA Panel Recommends Approval of ORKAMBI™ via Vertex

Yale scientists use gene editing to correct mutation in cystic fibrosis via Yale News

New antibiotic teixobactin kills drug-resistant superbugs, study says via LA Times

CFF Announces Unprecedented Acceleration and Expansion of CF Research, Care and Patient Programs

FDA Recommends Approval of KALYDECO for Use in People with CF R117H Mutation

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